Guided by science and dedicated to patients
is simple… bring innovative RNA modulating therapies to patients with genetic neurological diseases.
is to become a recognized leader in developing antisense oligonucleotide RNA modulators for genetic neurological disorders and to establish an organization that fosters positive and collaborative relationships with patients, physicians, partners, community members and our fellow employees.
Our core values (TRAITS)
guide our culture and govern our performance.
Teamwork will drive our success
Respect each other
Accountable for ourselves and our teams
Integrity will build trust
Serve patients and communities
Chief Executive Officer
Nicole Datson, PhD
Chief Scientific Officer / Site head
Chief Medical Officer
Board of Directors
Board Member (independent)
Co-Founder & Board Member
Founder & Board Member
We are proud to be supported by leading biotech investors