About

Guided by science and dedicated to patients

Our mission

is simple… bring innovative RNA modulating therapies to patients with genetic neurological diseases.

Our vision

is to become a recognized leader in developing antisense oligonucleotide RNA modulators for genetic neurological disorders and to establish an organization that fosters positive and collaborative relationships with patients, physicians, partners, community members and our fellow employees.

Our core values (TRAITS)

guide our culture and govern our performance.

Teamwork will drive our success
Respect each other
Accountable for ourselves and our teams
Integrity will build trust
Transparency
Serve patients and communities

 

Management Team

Micah Mackison

Micah Mackison

Chief Executive Officer

Nicole Datson, PhD

Nicole Datson, PhD

Chief Development Officer

Scott Schobel

Scott Schobel

Chief Medical Officer

Board of Directors

Anders Hinsby

Anders Hinsby

Board Member (independent)

Amy Schulman

Amy Schulman

Board Member

Klaus Breiner

Klaus Breiner

Board Member

Josh Mandel-Brehm

Josh Mandel-Brehm

Co-Founder & Board Member

Remi Droller

Remi Droller

Board Member

Felice Verduyn

Felice Verduyn

Board Member

Martijn Kleijwegt

Martijn Kleijwegt

Board Member

Luc Dochez

Luc Dochez

Founder & Board Member

Investors

We are proud to be supported by leading biotech investors