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Datson et al., Nucleic Acid Therapeutics 2020

https://pubmed.ncbi.nlm.nih.gov/31821107/

Bosgra et al., Nucleic Acid Therapeutics 2019

https://pubmed.ncbi.nlm.nih.gov/31429628/

Kourkouta_Mol Ther-Nuc Acids_2019_PS659 in SCA models

https://pubmed.ncbi.nlm.nih.gov/31394429/

Beekman et al., PLoS One, 2018; 13(4): e0195850

https://pubmed.ncbi.nlm.nih.gov/29641567/

González-Barriga et al., Nucleic Acis Therapeutics 2017

https://pubmed.ncbi.nlm.nih.gov/28375678/

Datson et al., PLoS One. 2017; 12(2): e0171127

https://pubmed.ncbi.nlm.nih.gov/28182673/
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